Beta-Thalassemia in India: A Growing Health Burden and the Promise of Gene Therapy
Blood disorders continue to pose a significant global health challenge, particularly in regions where inherited conditions are common. Among these, β-thalassemia stands out as one of the most serious and lifelong genetic diseases affecting millions worldwide. In India, the burden is especially high, making it not just a medical issue but a public health priority […]
Spinal Muscular Atrophy: From Genes to Therapies
Understanding a Rare Neuromuscular Disease Spinal muscular atrophy (SMA) is a genetic disorder that causes muscle weakness and atrophy. It is characterized by the progressive loss of motor neurons, which are the nerve cells that control muscle movement. These neurons control voluntary muscle movements, including those involved in walking, swallowing, and breathing. Without sufficient SMN […]